GEN VA HUJAYRA TERAPIYASINING ZAMONAVIY TIBBIYOTDAGI ISTIQBOLLARI
DOI:
https://doi.org/10.5281/Keywords:
gen terapiyasi, hujayra terapiyasi, gen tahrirlash, CRISPR/Cas9, ildiz hujayralari, CAR-T, regenerativ tibbiyot, biotexnologiya.Abstract
Gen va hujayra terapiyasi zamonaviy tibbiyotning jadal rivojlanayotgan innovatsion yo‘nalishlaridan biridir. Ushbu texnologiyalar irsiy, onkologik, immunologik va ayrim degenerativ kasalliklarni davolashda yangi imkoniyatlarni yaratmoqda. Gen terapiyasining asosiy maqsadi kasallik rivojlanishiga sabab bo‘luvchi genetik nuqsonni tuzatish, zararlangan gen faoliyatini o‘zgartirish yoki hujayraga terapevtik gen kiritishdan iborat. Hujayra terapiyasida esa bemorning o‘zidan yoki donordan olingan hujayralardan davolash maqsadida foydalaniladi. Hozirgi kunda genetik modifikatsiyalangan hujayralar, CAR-T terapiyasi, ildiz hujayralari va gen tahrirlash texnologiyalari klinik tibbiyotning muhim yo‘nalishlariga aylanmoqda. FDA ma’lumotlariga ko‘ra, gen va hujayra terapiyasining bir qator mahsulotlari allaqachon tasdiqlangan va yangi preparatlar klinik rivojlanishda davom etmoqda.
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